Publications

Insights

Identifying and engaging patients to enable precision medicine trials: A real world success story in a movement disorder setting.
“In February 2022, Skyler Jackson and Zack Denoma presented two posters at WORLDsymposium 2022. One poster is on a genetic testing program in a rare movement disorder and the other is about a methodology to conceptualize the burden of access in a rare lysosomal storage disorder. The team greatly enjoyed the opportunity to meet with industry partners and members from patient associations after working together virtually for such a long time.”