Understanding Burden of Access &
Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy (DMD) is a disease that affects 1/5,000 boys at birth worldwide. Boys are typically diagnosed at ages 3-5, typically lose the ability to walk at ages 8-12, and today there is no cure. Engage Health is in the midst of conducting a quantitative patient reported outcomes study under an ITB approval to document the patient experience in DMD as it relates to the burden experienced by patients and their families related to access to therapies as well as the burden to healthcare providers helping patients obtain access. If you are a DMD patient or family member, click here to participate. If you are a healthcare provider who assists DMD patients with insurance issues, click here to participate.