Fabry Disease Trial Recruitment

Fabry disease is a rare genetic, lysosomal storage disorder that affects an estimated 1 in 40,000 to 60,000 males. We are using the EnCompass™ database to recruit for the AVR-RD-01-201 trial, a study of an investigational ex-vivo gene therapy for Fabry disease. To determine efficacy, the researchers are looking for treatment-naïve males experiencing classic Fabry disease. Click here to determine if you or your patient qualifies.