Enhancing Awareness and Understanding of
Gene Therapy among Rare Disease Communities:A Research-Driven Roadmap
This study, conducted by Engage and its partner SmithSolve, formed a quantitative, nuanced picture of how the burgeoning field of gene therapy is understood and interpreted by key stakeholders, providing recommendations to improve communication and enhance awareness as this important technology transitions into the mainstream of rare disease treatment.
Enhancing Awareness and Understanding of Gene Therapy among Rare Disease Communities: A Research-Driven Roadmap (Smith C., Burns K., Engel P., Steinberg P.; 2015)